GondolaBio

Code Bio

This company develops non-viral genetic medicine delivery platforms and therapies for patients with rare and prevalent genetic diseases.

IntrepidiaBio

This biopharmaceutical company develops therapeutic products to address unmet medical needs for patients.

Scenic Biotech

This company develops disease-modifying small molecule therapeutics for patients with rare genetic and neurodegenerative disorders using its proprietary genetic modifier discovery platform.

Actio Biosciences

This biotechnology company develops small molecule medicines to treat rare genetic diseases and common conditions for patients with high unmet medical needs.

Bridge BIO

This biopharmaceutical company develops and provides medicines for patients with genetic diseases and cancers with clear genetic drivers.

Borea Therapeutics

The company develops bio-conjugated viral vectors for gene therapy to treat patients with genetic or chronic diseases.

Mahzi Therapeutics

This biotechnology company develops gene and antisense oligonucleotide therapies for patients with rare genetic neurodevelopmental disorders.

Strategic Partners

This company develops drug candidates for serious genetic disorders to serve patients with rare diseases.