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Ribonaut Therapeutics

Ribonaut Therapeutics develops small molecule drugs that target and degrade disease-causing RNA to treat neurological conditions and movement disorders for human patients.

Armatus

The company develops vectorized RNAi therapeutics to treat genetic neurological and neuromuscular diseases for patients with rare conditions.

Shape Therapeutics

The company develops programmable RNA medicines and delivery systems for patients with genetic disorders and other hard-to-treat diseases.

Biorchestra

The company develops RNA-based medicines and delivery systems for patients with neurodegenerative and rare central nervous system diseases.

Helex

This biotechnology company develops gene editing therapeutics and lipid nanoparticle delivery platforms for patients suffering from genetic kidney diseases.

HelixNano

This biotechnology company develops messenger RNA technologies and vaccines for patients with infectious diseases, cancer, and organ transplant needs.

Neurogene Inc

This company develops genetic medicines and gene therapies to treat patients and families affected by rare neurological diseases including Rett syndrome and Batten disease.

Vico Therapeutics

This company develops antisense oligonucleotide therapies to treat patients with rare genetic neurological disorders, including Huntington's disease and spinocerebellar ataxias.