Sentynl Therapeutics

Wilson Therapeutics AB

This biopharmaceutical company develops novel de-coppering therapies for patients with Wilson's disease to prevent liver and brain damage from toxic copper accumulation.

Sentinel Oncology

The company develops small molecule drug candidates to treat cancers and rare brain disorders for the pharmaceutical and biotechnology sectors.

Clementia

Clementia develops drugs for rare bone diseases, including fibrodysplasia ossificans progressiva, for patients with these life-altering conditions.

Reneo Pharmaceuticals

The company develops therapies for patients with rare genetic mitochondrial diseases that cause deficits in cellular metabolism and energy production.

Curzion Pharmaceuticals

This biopharmaceutical company develops oral small molecule therapies to treat patients with rare fibrotic conditions like diffuse cutaneous systemic sclerosis.

Scenic Biotech

This company develops disease-modifying small molecule therapeutics for patients with rare genetic and neurodegenerative disorders using its proprietary genetic modifier discovery platform.

Uncommon Therapeutics

This company develops gene-based medicines for patients with rare neurodevelopmental disorders, with an initial focus on treating Rett Syndrome.

Saol Therapeutics

This pharmaceutical company develops clinical-stage therapies for patients with central nervous system disorders, pain, spasticity and orphan diseases.