Anvesana

Armatus

The company develops vectorized RNAi therapeutics to treat genetic neurological and neuromuscular diseases for patients with rare conditions.

Shape Therapeutics

The company develops programmable RNA medicines and delivery systems for patients with genetic disorders and other hard-to-treat diseases.

Typewriter Therapeutics

The company develops RNA-based genetic medicines for patients with cancer, autoimmune conditions and rare genetic diseases.

Aptadir Therapeutics

The company develops RNA inhibitor-based therapeutics that reactivate silenced genes to treat patients with intractable cancers and rare genetic conditions.

Scenic Biotech

This company develops disease-modifying small molecule therapeutics for patients with rare genetic and neurodegenerative disorders using its proprietary genetic modifier discovery platform.

Adrestia

This company develops precision medicines for rare and common genetic diseases by using a molecular biology platform to identify and rescue cellular imbalances.

Airna

This company develops RNA editing therapeutics to treat patients with rare genetic and common cardiometabolic diseases.

SonoThera™

This company develops an ultrasound-guided non-viral platform to deliver genetic medicines for patients with chronic and rare diseases.