4D Molecular Therapeutics

4DMT

This company develops targeted gene therapy medicines for patients with severe genetic and retinal diseases.

AavantiBio

This digital health company develops gene transfer therapies for patients with rare genetic conditions including Friedreich's ataxia and cardiac diseases.

PulseSight Therapeutics

This company develops non-viral gene therapies for patients with severe eye diseases including age-related macular degeneration.

Adverum Biotechnologies

The company develops ocular gene therapies to treat retinal diseases for patients with vision-threatening conditions such as wet age-related macular degeneration.

Cirrus Therapeutics

This company develops gene and cell therapies to treat age-related macular degeneration and chronic vision loss for patients with blinding eye diseases.

Spot Biosystems

This company develops non-viral gene therapy delivery platforms using extracellular vesicles to treat genetic diseases for pharmaceutical partners and healthcare providers.

GenSight Biologics

This company develops gene therapies for patients suffering from neurodegenerative retinal diseases and central nervous system disorders.

Stridebio

This company develops engineered viral vectors and gene therapies for patients with rare genetic diseases.