Cerecor

Cereno Scientific

This biotech company develops epigenetic therapies for patients with rare cardiovascular and pulmonary diseases.

Ultragenyx

This biopharmaceutical company develops and commercialises therapies for patients with serious rare and ultra-rare genetic diseases.

SpringWorks Therapeutics

This biopharmaceutical company develops and commercialises targeted oncology medicines and therapies for patients with rare diseases and cancer.

ArQule

This biopharmaceutical company develops targeted small molecule drug candidates to treat cancers and rare diseases for patients with unmet medical needs.

Cerevel Therapeutics

This biopharmaceutical company develops neuroscience medicines for patients with mental and neurological conditions including schizophrenia, Parkinson's disease and epilepsy.

Eton Pharmaceuticals

This company develops and commercialises prescription medicines to treat patients living with rare diseases.

Pharos IBT

This company develops artificial intelligence platforms for discovering and developing treatments for rare and refractory diseases for the pharmaceutical and biotechnology industries.

Spero Therapeutics

This biopharmaceutical company develops medicines for patients with immune-mediated diseases and multidrug-resistant bacterial infections.