Alesta Therapeutics

Atavistik Bio

This biotechnology company develops oral allosteric small molecule therapeutics for patients with rare hematological diseases and cancers.

Tay Therapeutics

This biotech company develops small molecule oral gene therapies for patients with rare genetic disorders and inflammatory conditions through licensing and strategic partnerships.

Comet Therapeutics

This biotechnology company develops coenzyme A metabolism therapies to treat patients with inherited metabolic diseases and orphan neurological disorders.

Scenic Biotech

This company develops disease-modifying small molecule therapeutics for patients with rare genetic and neurodegenerative disorders using its proprietary genetic modifier discovery platform.

Adrestia

This company develops precision medicines for rare and common genetic diseases by using a molecular biology platform to identify and rescue cellular imbalances.

Mereo BioPharma

The company develops clinical-stage therapies for patients with rare diseases, including osteogenesis imperfecta and alpha-1 antitrypsin deficiency-associated lung disease.

Actio Biosciences

This biotechnology company develops small molecule medicines to treat rare genetic diseases and common conditions for patients with high unmet medical needs.

Edgewise

This biopharmaceutical company develops oral small molecule therapies to treat patients with rare skeletal and cardiac muscle diseases.