Forma Therapeutics

Forma

This company develops small molecule therapies for patients with sickle cell disease and cancer.

Imara

This biopharmaceutical company develops oral small-molecule therapies to treat patients with rare genetic blood disorders, including sickle cell disease and beta thalassemia.

Global Blood Therapeutics

This biopharmaceutical company develops and manufactures oral medicines to treat sickle cell disease for patients and healthcare providers.

Bluebird Bio

This company develops and manufactures gene therapies for patients with severe genetic diseases, including sickle cell disease and beta-thalassaemia.

Disc Medicine

This biopharmaceutical company develops novel therapeutic candidates to treat patients suffering from serious haematologic diseases by targeting red blood cell biology and iron homeostasis.

Shape Therapeutics

The company develops programmable RNA medicines and delivery systems for patients with genetic disorders and other hard-to-treat diseases.

Beam Therapeutics

The company develops precision genetic medicines using base editing technology to treat patients with serious genetic diseases such as sickle cell disease.

Kamau Therapeutics

This company develops clinical-stage gene correction therapies using targeted DNA integration to treat patients with sickle cell disease and other genetic conditions.