CureAge

Shape Therapeutics

The company develops programmable RNA medicines and delivery systems for patients with genetic disorders and other hard-to-treat diseases.

Neurogene Inc

This company develops genetic medicines and gene therapies to treat patients and families affected by rare neurological diseases including Rett syndrome and Batten disease.

CamGene

This company develops RNA-based therapeutics using lipid nanoparticle technology to treat hearing loss for patients with cellular dysfunction or undergoing cochlear implant surgery.

Coave Therapeutics

The company develops targeted gene therapies for patients with neurodegenerative and ocular diseases.

Spot Biosystems

This company develops non-viral gene therapy delivery platforms using extracellular vesicles to treat genetic diseases for pharmaceutical partners and healthcare providers.

CamGene Therapeutics

This biotechnology company develops RNA-based medicines and lipid nanoparticle delivery technologies to treat hearing loss for patients with cellular dysfunction or cochlear implants.

Uncommon Therapeutics

This company develops gene-based medicines for patients with rare neurodevelopmental disorders, with an initial focus on treating Rett Syndrome.

Helex

This biotechnology company develops gene editing therapeutics and lipid nanoparticle delivery platforms for patients suffering from genetic kidney diseases.