Encoded Therapeutics

Stoke Therapeutics

This biotechnology company develops antisense oligonucleotide medicines to treat severe genetic diseases by restoring protein expression for patients with conditions such as Dravet syndrome.

Neurosciences

This company develops precision sodium channel therapeutics to treat patients with neurological conditions such as genetic epilepsy and chronic neuropathic pain.

Neurogene Inc

This company develops genetic medicines and gene therapies to treat patients and families affected by rare neurological diseases including Rett syndrome and Batten disease.

EpilepsyGTx

This company develops precision gene therapies for patients with focal refractory epilepsy to provide seizure freedom.

Uncommon Therapeutics

This company develops gene-based medicines for patients with rare neurodevelopmental disorders, with an initial focus on treating Rett Syndrome.

Lario Therapeutics

This company develops precision medicines for patients with severe neurological disorders, including epilepsy and Parkinson’s disease.

Navion

This biotechnology company develops precision sodium channel medicines for patients with neurological conditions including genetic epilepsy and chronic neuropathic pain.

Neumirna Therapeutics

This biotechnology company develops microRNA-based therapies to treat patients with neurological disorders, including drug-resistant epilepsy and Parkinson's disease.