HRMY

Harmony Biosciences

This pharmaceutical company develops and commercialises therapies for patients living with rare neurological diseases, such as narcolepsy and other sleep-wake disorders.

Noema Pharma

This company develops clinical-stage therapeutic products for patients with central nervous system disorders and orphan neurological conditions.

Eton Pharmaceuticals

This company develops and commercialises prescription medicines to treat patients living with rare diseases.

ALMS

This biopharmaceutical company develops oral therapies to treat patients with immune-mediated diseases, neuroinflammatory conditions and neurodegenerative disorders.

Ultragenyx

This biopharmaceutical company develops and commercialises therapies for patients with serious rare and ultra-rare genetic diseases.

Abliva

This biopharmaceutical company develops novel medicines for patients suffering from rare and severe primary mitochondrial diseases.

Herantis Pharma

This clinical-stage biotechnology company develops neurorestorative drug therapies for patients living with Parkinson's disease.

PHVS

This company develops oral therapies to treat and prevent hereditary angioedema attacks for patients with rare diseases.