Minoryx

Minoryx Therapeutic

This biotech company develops therapies for orphan central nervous system diseases, such as X-linked adrenoleukodystrophy, for patients with high unmet medical needs.

Minoryx Therapeutics

This company develops leriglitazone, a pharmacological treatment for patients with rare genetic central nervous system diseases such as X-linked adrenoleukodystrophy.

Noema Pharma

This company develops clinical-stage therapeutic products for patients with central nervous system disorders and orphan neurological conditions.

Mahzi Therapeutics

This biotechnology company develops gene and antisense oligonucleotide therapies for patients with rare genetic neurodevelopmental disorders.

Scenic Biotech

This company develops disease-modifying small molecule therapeutics for patients with rare genetic and neurodegenerative disorders using its proprietary genetic modifier discovery platform.

Pheno Therapeutics

This biotech company develops neuroprotective and remyelinating therapies for patients with multiple sclerosis and other neurodegenerative disorders.

AveXis

This biotechnology firm develops gene therapies for patients with rare and life-threatening neurological genetic diseases including spinal muscular atrophy.

NeurOdys Therapeutics

This biotechnology company develops small molecule therapies for patients with neurodegenerative conditions such as Alzheimer's and Parkinson's diseases.