AAVantgarde Bio

AAVantgarde

This biotechnology company develops gene therapies for patients with inherited retinal diseases, such as Stargardt disease and Usher syndrome type 1B.

Coave Therapeutics

The company develops targeted gene therapies for patients with neurodegenerative and ocular diseases.

SpliceBio

The company develops gene therapies using protein splicing technology to deliver large genes for patients with genetic diseases such as Stargardt disease.

Adverum Biotechnologies

The company develops ocular gene therapies to treat retinal diseases for patients with vision-threatening conditions such as wet age-related macular degeneration.

Sparing Vision

This genomic medicine company develops mutation-agnostic gene therapies to preserve and restore sight for patients with blinding inherited retinal diseases.

Ikarovec

This company develops bicistronic gene therapies to treat chronic ophthalmic diseases, such as age-related macular degeneration, for patients suffering from vision loss.

Atsena

This clinical-stage gene therapy company develops genetic medicines to reverse or prevent blindness for patients with inherited retinal diseases.

Nightstar

This company develops gene therapies for patients with rare inherited retinal diseases that cause progressive blindness.