Allena

OxThera AB

This biopharmaceutical company develops bacteria-based therapies to treat patients with primary hyperoxaluria and other rare kidney diseases.

Allievex

This clinical-stage biotechnology company develops enzyme replacement therapies for children with rare pediatric neurodegenerative diseases, specifically Sanfilippo syndrome type B.

Alnara

The company develops protein therapeutics to treat metabolic diseases, such as exocrine pancreatic insufficiency, for patients with conditions including cystic fibrosis and chronic pancreatitis.

Alesta Therapeutics

This biotechnology company develops oral small molecule therapies for patients with rare genetic disorders including hypophosphatasia and Charcot-Marie-Tooth disease.

ENYO Pharma

This digital health company develops small molecule therapeutics to treat patients with chronic kidney diseases and rare conditions like Alport syndrome.

Sidera

This company develops small molecule medicines for patients with metabolic, inflammatory and kidney diseases using human genetic research findings.

Alcresta

This company manufactures enzyme-based cartridges for enteral feeding tubes to assist fat absorption in patients with rare diseases and pancreatic insufficiency.

Airna

This company develops RNA editing therapeutics to treat patients with rare genetic and common cardiometabolic diseases.