Marathon Pharmaceuticals

Noema Pharma

This company develops clinical-stage therapeutic products for patients with central nervous system disorders and orphan neurological conditions.

Saol Therapeutics

This pharmaceutical company develops clinical-stage therapies for patients with central nervous system disorders, pain, spasticity and orphan diseases.

Marinus Pharmaceuticals

This pharmaceutical company produces ganaxolone, an oral suspension treatment for seizures in adult and paediatric patients with rare genetic epilepsy disorders.

Mahzi Therapeutics

This biotechnology company develops gene and antisense oligonucleotide therapies for patients with rare genetic neurodevelopmental disorders.

Actelion

This company develops and manufactures pharmaceutical drugs to treat orphan diseases such as pulmonary arterial hypertension for patients and healthcare providers globally.

Civitas Therapeutics

This biopharmaceutical company develops inhaled drug delivery technologies for patients with neurological disorders such as Parkinson's disease.

Biohaven

This biopharmaceutical company develops therapeutics for patients with debilitating neurological, neuroinflammatory, and metabolic diseases, as well as immunological and oncology disorders.

Minoryx

This biotechnology company develops orphan drugs and therapies for patients suffering from rare, life-threatening genetic diseases of the central nervous system.