株式会社ONODERA GT Pharma

EpilepsyGTx

This company develops precision gene therapies for patients with focal refractory epilepsy to provide seizure freedom.

Prevail Therapeutics

The company develops adeno-associated virus gene therapies to treat patients with neurodegenerative conditions including Parkinson's disease and frontotemporal dementia.

Spur Therapeutics

This company develops adeno-associated virus gene therapies to treat chronic conditions including Gaucher disease and Parkinson's disease for patients with inherited genetic disorders.

EveryONE Medicines

The company develops individualized antisense oligonucleotide therapies for children with rare life-threatening neurodegenerative diseases caused by unique genetic mutations.

Eikonoklastes Therapeutics

This clinical stage biopharmaceutical company develops gene therapies for patients suffering from amyotrophic lateral sclerosis and other neurodegenerative diseases.

Meira GTX

This company develops genetic therapies and gene regulation technologies for patients with rare and prevalent diseases including Parkinson’s and inherited retinal disorders.

Scripta Therapeutics

The company develops therapeutics that modulate transcription factor activity to treat neurodegenerative diseases for patients with conditions such as Alzheimer's and Parkinson's.

Coave Therapeutics

The company develops targeted gene therapies for patients with neurodegenerative and ocular diseases.