Meira GTX

GenSight Biologics

This company develops gene therapies for patients suffering from neurodegenerative retinal diseases and central nervous system disorders.

Freeline

This company develops gene therapies for patients with Gaucher disease, Parkinson’s disease and other chronic conditions.

Neurogene Inc

This company develops genetic medicines and gene therapies to treat patients and families affected by rare neurological diseases including Rett syndrome and Batten disease.

EpilepsyGTx

This company develops precision gene therapies for patients with focal refractory epilepsy to provide seizure freedom.

Spur Therapeutics

This company develops adeno-associated virus gene therapies to treat chronic conditions including Gaucher disease and Parkinson's disease for patients with inherited genetic disorders.

Uncommon Therapeutics

This company develops gene-based medicines for patients with rare neurodevelopmental disorders, with an initial focus on treating Rett Syndrome.

Prevail Therapeutics

The company develops adeno-associated virus gene therapies to treat patients with neurodegenerative conditions including Parkinson's disease and frontotemporal dementia.

Beacon Therapeutics

This company develops ophthalmic gene therapies to restore vision for patients with rare and prevalent retinal diseases causing blindness.