Spur Therapeutics

Freeline

This company develops gene therapies for patients with Gaucher disease, Parkinson’s disease and other chronic conditions.

Genespire

This company develops off-the-shelf gene therapies for children and adults affected by inherited metabolic diseases and primary immunodeficiencies.

Stridebio

This company develops engineered viral vectors and gene therapies for patients with rare genetic diseases.

Spot Biosystems

This company develops non-viral gene therapy delivery platforms using extracellular vesicles to treat genetic diseases for pharmaceutical partners and healthcare providers.

Prevail Therapeutics

The company develops adeno-associated virus gene therapies to treat patients with neurodegenerative conditions including Parkinson's disease and frontotemporal dementia.

Neurogene Inc

This company develops genetic medicines and gene therapies to treat patients and families affected by rare neurological diseases including Rett syndrome and Batten disease.

Meira GTX

This company develops genetic therapies and gene regulation technologies for patients with rare and prevalent diseases including Parkinson’s and inherited retinal disorders.

Sania Therapeutics

This company develops controllable gene therapies for patients with neurological disorders caused by dysfunctional neural circuits, specifically targeting motor conditions like spasticity.