Genetix Biotherapeutics

Bluebird Bio

This company develops and manufactures gene therapies for patients with severe genetic diseases, including sickle cell disease and beta-thalassaemia.

Imara

This biopharmaceutical company develops oral small-molecule therapies to treat patients with rare genetic blood disorders, including sickle cell disease and beta thalassemia.

Kamau Therapeutics

This company develops clinical-stage gene correction therapies using targeted DNA integration to treat patients with sickle cell disease and other genetic conditions.

Forma Therapeutics

This company develops medicines for patients with sickle cell disease and rare blood disorders.

Orchard Therapeutics

Orchard Therapeutics develops haematopoietic stem cell gene therapies for patients living with severe genetic diseases.

Seamless Therapeutics

The company develops programmable recombinase-based gene editing therapies for patients with severe genetic diseases through its proprietary technology platform.

Spur Therapeutics

This company develops adeno-associated virus gene therapies to treat chronic conditions including Gaucher disease and Parkinson's disease for patients with inherited genetic disorders.

Salve Therapeutics

The company develops a bioengineering platform for designing and testing viral gene therapies to treat genetic disorders for biotechnology and pharmaceutical organisations.