Freeline

Spur Therapeutics

This company develops adeno-associated virus gene therapies to treat chronic conditions including Gaucher disease and Parkinson's disease for patients with inherited genetic disorders.

Meira GTX

This company develops genetic therapies and gene regulation technologies for patients with rare and prevalent diseases including Parkinson’s and inherited retinal disorders.

Prevail Therapeutics

The company develops adeno-associated virus gene therapies to treat patients with neurodegenerative conditions including Parkinson's disease and frontotemporal dementia.

Bluebird Bio

This company develops and manufactures gene therapies for patients with severe genetic diseases, including sickle cell disease and beta-thalassaemia.

Purespring Therapeutics

This company develops gene therapies for patients with chronic renal diseases to preserve kidney function and treat conditions like IgA nephropathy.

Alia Therapeutics

The company develops gene editing medicines for patients with genetic diseases.

Genetix Biotherapeutics

The company develops and commercialises gene therapies for patients suffering from severe rare genetic disorders such as sickle cell disease and beta thalassemia.

Anjarium BioSciences

This company develops non-viral gene therapies and synthetic DNA vectors for patients with genetic diseases and life sciences researchers.